FDA approves another rare blood disorder treatment, sickle cell treatment on its way
The U.S. Food and Drug Administration last week approved a genetic treatment for the blood disorder beta-thalassemia, marking the third U.S. gene therapy for a rare disease. www.science.org/content/article/news-glance-new-gene-therapy-europe-s-drought-and-black-hole-s-photon-ring? The disorder causes low haemoglobin and severe anaemia, and the regular blood transfusions used to treat it can cause iron build-up that damages organs. The new treatment, …
FDA approves another rare blood disorder treatment, sickle cell treatment on its way Read More »
